Critical bottlenecks in rare disease research and care: A community perspective

McMurry J, Sizer A, Allaway R, Boerkoel C, Chen AJ, Colquitt J, Cummings J, Dutta A, Fitter N, Green RC, Hanson A, Harker E, Harris N, Hovinga C, Kahn A, Keil H, Kessler R, Lange L, Loaiza-Bonilla A, Luchkina N, Luellen E, Movaghar A, Pastinen T, Rountree E, Rudrapatna V, Sand A, Schmolly K, Short P, Sirota M, Siwo G, Tatonetti N, Vidra N, Vij F, Volchenboum S, Walden A, Walls RL, Washington P, Wenzlau D, Wenzlau M, Wheeler M, Son Rigby C, Haendel M